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/Compositions And Methods Comprising Small Nuclear Rna (snrna) For Treating Dmd
Abstract

SnRNA systems targeting DMA RNA sequences are disclosed herein.

Full Text

What is claimed is:

SnRNA systems targeting DMA RNA sequences are disclosed herein.
Timeline
Filed
03/24/2026
Published
07/16/2026
Granted
Not Available
IPC Codes(2)
C12N 15/113:Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides
C12N 15/86:Viral vectors