Abstract
Disclosed herein are polynucleic acid molecules, pharmaceutical compositions, and methods for treating muscle dystrophy (DM1).
Full Text
What is claimed is:
Disclosed herein are polynucleic acid molecules, pharmaceutical compositions, and methods for treating muscle dystrophy (DM1).
Timeline
Filed
05/05/2026Published
08/27/2026Granted
Not AvailableIPC Codes(2)
A61K 47/68:the modifying agent being an antibody, an immunoglobulin or a fragment thereof, e.g. an Fc-fragment
C12N 15/113:Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides